Tag: Duchenne
As Sarepta, FDA tangle over Duchenne therapy, families are caught in the middle
Jennifer Hill Blair was in the middle of a school meeting when she saw the Cincinnati number pop…
Sarepta will stop shipping Elevidys, Duchenne gene therapy
Sarepta Therapeutics made a surprising announcement on Monday evening, revealing that it will be pausing all shipments of…
Duchenne muscular dystrophy community rocked by Sarepta death
The tragic death of a second teenage boy from liver failure caused by a gene therapy from Sarepta…
The Triumphs And Trials Of Duchenne Gene Therapy
Gene therapy has been making significant strides in changing the narrative for children with genetic diseases like Duchenne…
Dispute over Duchenne treatment highlights thorny access issues
Sarah Jenssen had been waiting for a ray of hope in her battle against Duchenne muscular dystrophy, a…