Tag: gene
Second Patient Death After Gene Therapy: Implications For The Future
Gene therapy, a groundbreaking field of medicine, is currently facing a critical juncture following the tragic deaths of…
The Triumphs And Trials Of Duchenne Gene Therapy
Gene therapy has been making significant strides in changing the narrative for children with genetic diseases like Duchenne…
Gene editing could treat damage from ‘irreversible’ kidney disease
Kidney Disease Reversed in Animal Studies Using CRISPR Gene Editing Kidney disease can lead to high blood pressure…
FDA hints relaxed rules are coming for rare disease gene therapy
The Trump administration's impact on gene therapy was a topic of discussion at a recent FDA "Cell and…
Gene Therapy For Inherited Disease In The Unborn Child
In the realm of genetic medicine, a groundbreaking shift is occurring that promises to revolutionize the way we…
Gene Therapy For Inherited Disease In Infants
Advances in medical technology have revolutionized the way we approach inherited diseases, especially in infants. With newborn screening…
Personalized gene editing saved a baby, but the tech’s future is uncertain
The gene therapy involved editing KJ’s own cells to correct the mutation in his CPS1 gene. The therapy…
What Baby KJ means for future of CRISPR gene editing industry
The gene editing industry has faced numerous challenges in recent years, with layoffs, closures, and sinking stock prices…
ASGCT news: Baby KJ and the dream of personalized gene editing
In a groundbreaking announcement at the ASGCT conference in New Orleans, Kiran Musunuru, a researcher at the University…
Baby with rare disease given world-first personal CRISPR gene therapy
A Glimpse into the Future of Medicine: Baby Receives Bespoke CRISPR Gene-Editing Treatment Baby KJ after a gene-editing…
Day 1 at ASGCT: Missing scientists, a gene editing failure, and a gene editing first
The atmosphere at the annual meeting of the American Society of Cell and Gene Therapy in New Orleans…
As financial prospects for gene therapies dim, ambitious charity steps up
The Telethon Foundation in Milan has been a longstanding supporter of research for genetic diseases, funding various projects…